Sectors / Genomics & Medicine

Biology becomes
engineering.

Sequencing is cheap. Gene editing is precise. AI is reading the genome. R2A tracks 44 names across RNA therapeutics, gene editing, sequencing, AI-driven drug discovery, and the rare-disease franchises that pay for the platforms.

44
Names covered
23
Buy calls
19
Hold
0
Private comps
Illustration: the readable genome

The Thesis

The cost of sequencing a human genome has fallen from $1B in 2001 to under $200 today. CRISPR was a Nobel Prize in 2020; in 2026 there's an approved cure for sickle cell on the market and base-editing trials in the clinic. AI-driven drug discovery is no longer a slide-deck story — Schrödinger and Recursion have real partnerships, real candidates, and the early molecules are working their way through trials. The pieces that used to be theoretical are now operational.

R2A's variant view: the public-market opportunity is bifurcated. On one side, the platform companies (Alnylam, Arrowhead, Ionis, Vertex) have validated their delivery technology and now have approved drugs funding the next wave. On the other side, the moonshots (Beam, Intellia, CRISPR Therapeutics, Krystal) are binary on clinical readouts but the underlying biology is real. R2A weights more heavily toward the platforms — moonshot exposure should be sized as optionality, not core. The biggest sector by Buy count (23 of 44), and the one where R2A's variant view differs most from a typical generalist.

The Names

All Buy Hold Gene Editing RNA Therapeutics Sequencing
ALNY
Buy Conviction High
Alnylam · RNAi Therapeutics
The RNAi platform that actually worked. Five approved drugs, growing revenue, and the pipeline is the option on the next decade of rare-disease economics.
Scenario range
$220$372$460$580
BearBaseBullMoon
Last price$300.64
R2A fair value$372
VKTX
Buy Conviction High
Viking Therapeutics · Oral GLP-1 / Obesity
Oral GLP-1 is the holy grail vs. injectables. Phase 2 data was clean. Phase 3 starting. If it works at scale, Viking is the only credible follow-on franchise behind Lilly and Novo.
Scenario range
$10$56$95$140
BearBaseBullMoon
Last price$31.01
R2A fair value$56
NTLA
Buy Conviction High
Intellia · In-Vivo Gene Editing
In-vivo CRISPR delivered systemically — no cell extraction, no manufacturing complexity. NTLA-2002 in Phase 3 for ATTR. If it works, the entire economics of gene editing change.
Scenario range
$5$28$40$54
BearBaseBullMoon
Last price$13.41
R2A fair value$28.40
INSM
Buy Conviction High
Insmed · Rare Pulmonary
Arikayce franchise compounding plus brensocatib (bronchiectasis, NTM) reading out positively. Multiple shots on goal in pulmonary; rare-disease pricing.
Scenario range
$75$219$295$380
BearBaseBullMoon
Last price$133.26
R2A fair value$219
BEAM
Hold Conviction Medium
Beam Therapeutics · Base Editing
Base editing without making double-strand breaks. The platform that could replace first-gen CRISPR. BEAM-101 in sickle cell is the first big readout that matters.
Scenario range
$12$85$140$220
BearBaseBullMoon
Last price$30.70
R2A fair value$85
TEM
Buy Conviction Medium
Tempus AI · AI-Powered Diagnostics
The most credible AI diagnostics play. Real clinical data partnerships, real revenue, and the data moat gets deeper every year.
Scenario range
$22$75$120$180
BearBaseBullMoon
Last price$55.00
R2A fair value$75.50

Full Coverage

Every name R2A tracks in Genomics & Medicine. Click any column header to sort.

Ticker Company Call Conviction Last R2A FV Moon
ALNY
Alnylam
RNAi Therapeutics
Buy●●● High$300.64$372.00
ARWR
Arrowhead
RNAi Platform (TRiM)
Buy●●● High$74.15$100.00$180
ILMN
Illumina
Genomic Sequencing
Buy●●● High$136.81$150.00
INSM
Insmed
Rare Pulmonary
Buy●●● High$133.26$219.00
LEGN
Legend Biotech
BCMA CAR-T (Carvykti)
Buy●●● High$23.59$44.00
NTLA
Intellia
In-Vivo Gene Editing
Buy●●● High$13.41$28.40$54
RVMD
Revolution Medicines
KRAS / RAS Franchise
Buy●●● High$145.73$181.00
TGTX
TG Therapeutics
MS / Anti-CD20
Buy●●● High$33.85$44.20
TVTX
Travere Therapeutics
Rare Kidney
Buy●●● High$44.12$70.00
VKTX
Viking Therapeutics
Oral GLP-1 / Obesity
Buy●●● High$31.01$56.00
ABSI
Absci
AI-Driven Drug Discovery
Buy●● Medium$5.22$8.75
AXSM
Axsome
Neuro / Psych
Buy●● Medium$206.53$220.00
CRSP
CRISPR Therapeutics
Gene Editing
Buy●● Medium$50.31$82.00
GH
Guardant Health
Liquid Biopsy
Buy●● Medium$87.60$116.00
IMVT
Immunovant
FcRn / Autoimmune
Buy●● Medium$27.12$49.00
IONS
Ionis Pharmaceuticals
Antisense Therapeutics
Buy●● Medium$75.28$97.00
KRYS
Krystal Biotech
Gene Therapy (EB)
Buy●● Medium$266.04$290.00
LNTH
Lantheus
Radiopharm Diagnostic
Buy●● Medium$85.50$51.00
NTRA
Natera
Cell-Free DNA Testing
Buy●● Medium$207.28$248.00
SDGR
Schrödinger
Computational Drug Design
Buy●● Medium$12.76$15.21
SMMT
Summit Therapeutics
Bispecific Oncology
Buy●● Medium$16.12$39.60
TEM
Tempus AI
AI-Powered Diagnostics
Buy●● Medium$55.00$75.50
TWST
Twist Bioscience
Synthetic Biology
Buy●● Medium$59.73$53.03
ALT
Altimmune
GLP-1 dual / NASH
Hold●● Medium$2.82$5.34
BEAM
Beam Therapeutics
Base Editing
Hold●● Medium$30.70$85.00
BMRN
BioMarin
Rare Disease / Gene Therapy
Hold●● Medium$54.06$76.00
BNTX
BioNTech
mRNA / Oncology
Hold●● Medium$97.54$131.00
RARE
Ultragenyx
Rare Disease / Gene Therapy
Hold●● Medium$24.77$38.00
ABCL
AbCellera Biologics
AI Antibody Discovery
Hold●● Low$4.43$5.00
AKTS
Aktis Oncology
Targeted Radiopharm
Hold●● Low$19.42$34.00
APLS
Apellis
Complement Inhibition
Hold●● Low$40.96$40.00
DNLI
Denali Therapeutics
Neurodegeneration
Hold●● Low$18.30$25.00
EDIT
Editas Medicine
Gene Editing
Hold●● Low$2.90$3.22
IOVA
Iovance Biotherapeutics
Cell Therapy
Hold●● Low$3.40$5.50
LNZA
LanzaTech Global
Synthetic Biology / Carbon
Hold●● Low$24.78$22.00
MRNA
Moderna
mRNA Platform
Hold●● Low$45.37$62.00
PACB
PacBio
Long-Read Sequencing
Hold●● Low$1.60$2.23
PRME
Prime Medicine
Prime Editing
Hold●● Low$3.41$5.50
RLAY
Relay Therapeutics
Structure-Based Drug Design
Hold●● Low$12.72$13.00
RXRX
Recursion Pharmaceuticals
AI Drug Discovery
Hold●● Low$3.39$5.50
SANA
Sana Biotechnology
Engineered Cell Therapy
Hold●● Low$3.27$5.50
SRPT
Sarepta Therapeutics
Gene Therapy (DMD)
Hold●● Low$21.49$27.00
VCNX
Vaccinex
Immuno-Oncology
Sell●●● High$0.78$0.85
WGS
GeneDx (Sema4)
Genomic Diagnostics
Sell●● Low$34.20$54.00